New Drug for Muscular Dystrophy

Sat Oct 21 17:10:17 -0700 2006
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A new drug called PTC124 has just gone through some trials and had good success with a form of MD called Duchenne Musuclar Dystrophy.


..."According to data presented today at an international DMD conference in London, in a study of 26 boys with DMD who took PTC124 by mouth for 28 days, significant biochemical improvements were observed, and parents and teachers reported functional improvements in some of the participants. The data were from clinical trial sites at Children’s Hospital of Philadelphia, Cincinnati Children’s Hospital Medical Center and the University of Utah in Salt Lake City."...more there